专利 - 详情

专利名称	For treatment of central nervous system disorders of composition and method
申请号	JP2018529257	申请日
公开（公告）号	JP2019500349A	公开（公告）日	2016-12-14
申请（专利权）人		发明人	アズナレズイザベル; ナッシュヒューエム
专利来源	国家知识产权局	转化方式
摘要	Provided herein are methods and compositions for increasing the expression of ATP1A2, CACNA1A, SETD5, SHANK3, NF2, DNMT1, TCF4, RAI1, PEX1, ARSA, EIF2B5, EIF2B1, EIF2B2, NPC1, ADAR, MFSD8, STXBP1, PRICKLE2, PRRT2, IDUA, or STX1B, and for treating a subject in need thereof, e.g., a subject with deficient ATP1A2, CACNA1A, SETD5, SHANK3, NF2, DNMT1, TCF4, RAI1, PEX1, ARSA, EIF2B5, EIF2B1, EIF2B2, NPC1, ADAR, MFSD8, STXBP1, PRICKLE2, PRRT2, IDUA, or STX1B protein expression. 1人已参与 0数据匹配