专利名称 | OLIGONUCLEOTIDES TO TREAT EYE DISEASE. | ||
申请号 | MX2018013003 | 申请日 | |
公开(公告)号 | MX2018013003A | 公开(公告)日 | 2017-04-25 |
申请(专利权)人 | 发明人 | HEE LAM CHAN; HESTER CATHARINA VAN DIEPEN; JANNE JUHA TURUNEN | |
专利来源 | 国家知识产权局 | 转化方式 | |
摘要 |
The invention relates to the fields of medicine and immunology. In particular, it relates to novel antisense oligonucleotides that may be used in the treatment, prevention and/or delay of Usher Syndrome type II and/or USH2A-associated non syndromic retina degeneration, especially by skipping a pseudo exon (PE40) between exon 40 and 41 in the human USH2Agene. |
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