| 专利名称 | ECTOPICALLY EXPRESSED TRANSCRIPTION FACTORS AND USES THEREOF | ||
| 申请号 | WOEP18086782 | 申请日 | |
| 公开（公告）号 | WO2019122425A1 | 公开（公告）日 | |
| 申请（专利权）人 | FONDAZIONE TELETHON | 发明人 | SURACE Enrico Maria; BOTTA Salvatore; MARROCCO Elena; DE PRISCO Nicola |
| 专利来源 | 国家知识产权局 | 转化方式 | |
| 摘要 |
The present invention relates to a nucleic acid construct allowing to drives the expression of a transcription factor in rod cells or cone cells thereby silencing the expression of a gene which mutated form is responsible for a retinal dystrophy and its medical use, relative expression 5 vector, host cell, viral particle and pharmaceutical composition. |
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主管部门：海南中小企业服务 | 建设单位：海南商业联合会
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