专利名称 | TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS AND DISORDERS ASSOCIATED WITH THE SPINAL CORD | ||
申请号 | WOUS19040230 | 申请日 | |
公开(公告)号 | WO2020010042A1 | 公开(公告)日 | |
申请(专利权)人 | VOYAGER THERAPEUTICS INC | 发明人 | SAH Dinah Wen Yee; CHEN Qingmin; CARROLL Jenna; PATZKE Holger; HOU Jinzhao; HERSCH Steven M |
专利来源 | 国家知识产权局 | 转化方式 | |
摘要 |
The present disclosure relates to AAVs encoding a SOD1 targeting polynucleotide which may be used to treat amyotrophic lateral sclerosis (ALS) and delivery methods for the treatment of spinal cord related disorders including ALS. |
主管部门:海南中小企业服务 | 建设单位:海南商业联合会
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